Gene Therapy for Blindness Caused by Choroideremia
Condition(s):ChoroideremiaLast Updated:November 17, 2017Completed
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Condition(s):ChoroideremiaLast Updated:November 17, 2017Completed
Condition(s):Usher Syndrome; Congenital Deafness; Retinitis PigmentosaLast Updated:April 3, 2019Completed
Condition(s):Inherited Retinal Dystrophy Due to RPE65 MutationsLast Updated:February 26, 2024Active, not recruiting
Condition(s):Retinal Degeneration; Retinitis Pigmentosa; Eye Diseases, HereditaryLast Updated:November 29, 2023Active, not recruiting
Condition(s):Retinitis Pigmentosa; Age-related Macular Degeneration; Optic Nerve Pathology; Inherited Retinal DystrophiesLast Updated:June 13, 2019Completed
Condition(s):Usher Syndrome; Retinitis Pigmentosa; Congenital Hearing ImpairmentLast Updated:June 24, 2005Completed
Condition(s):Retinitis Pigmentosa; Stargardt Disease 1; Best Disease; Pattern Dystrophy of Macula; ChoroideremiaLast Updated:March 15, 2022Recruiting
Condition(s):Retinal DisorderLast Updated:February 24, 2023Withdrawn
Condition(s):Multiple Sclerosis; Optic NeuritisLast Updated:August 28, 2019Unknown status
Condition(s):ComplicationsLast Updated:April 22, 2016Completed
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