Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)
Condition(s):X-linked Severe Combined Immunodeficiency (XSCID)Last Updated:March 27, 2024Recruiting
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Condition(s):X-linked Severe Combined Immunodeficiency (XSCID)Last Updated:March 27, 2024Recruiting
Condition(s):Gene TherapyLast Updated:March 27, 2020Recruiting
Condition(s):Severe Combined Immunodeficiency, X-LinkedLast Updated:October 12, 2023Recruiting
Condition(s):Chronic Granulomatous Disease (CGD); X-Linked Severe Combined Immune Deficiency (XSCID); Leukocyte Adhesion Deficiency 1 (LAD); Graft Versus Host Disease (cGvHD)Last Updated:March 13, 2024Recruiting
Condition(s):Duchenne Muscular DystrophyLast Updated:March 22, 2021Recruiting
Condition(s):Lesch-Nyhan SyndromeLast Updated:September 21, 2022Recruiting
Condition(s):Muscular Dystrophy; Duchenne Muscular Dystrophy; Becker Muscular DystrophyLast Updated:February 9, 2023Not yet recruiting
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