The Natural History of Metachromatic Leukodystrophy Study (HOME Study)
Condition(s):Metachromatic LeukodystrophyLast Updated:June 13, 2023Active, not recruiting
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Condition(s):Metachromatic LeukodystrophyLast Updated:June 13, 2023Active, not recruiting
Condition(s):Duchenne Muscular DystrophyLast Updated:May 17, 2021Terminated
Condition(s):Genetic DiseaseLast Updated:March 26, 2024Recruiting
Condition(s):AlkaptonuriaLast Updated:May 31, 2018Unknown status
Condition(s):Angioedema; Angioedemas, Hereditary; Urticaria; Mastocytosis; ACE Inhibitor-Induced Angioedema; C1 Inhibitor Deficiency; Systemic Mastocytoses; Indolent Systemic MastocytosisLast Updated:January 18, 2024Not yet recruiting
Condition(s):Duchenne Muscular DystrophyLast Updated:January 13, 2023Recruiting
Condition(s):Becker Muscular DystrophyLast Updated:December 13, 2023Active, not recruiting
Condition(s):DMD; Duchenne Muscular Dystrophy; Duchenne; Exon 44Last Updated:February 6, 2024Enrolling by invitation
Condition(s):Undiagnosed Disease; Rare DiseasesLast Updated:March 12, 2024Enrolling by invitation
Condition(s):Nonsene Mutation Duchenne Muscular DystrophyLast Updated:September 21, 2023Completed
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