Gene Transfer Clinical Trial for Krabbe Disease
Condition(s):Krabbe DiseaseLast Updated:January 10, 2024Active, not recruiting
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Condition(s):Krabbe DiseaseLast Updated:January 10, 2024Active, not recruiting
Condition(s):Tay-Sachs Disease; Sandhoff DiseaseLast Updated:December 14, 2023Active, not recruiting
Condition(s):Gaucher’s DiseaseLast Updated:January 23, 2024Completed
Condition(s):Fabry DiseaseLast Updated:October 14, 2021Recruiting
Condition(s):Metachromatic LeukodystrophyLast Updated:June 13, 2023Active, not recruiting
Condition(s):Gangliosidoses; GM1 Gangliosidosis; Morquio B Disease; Sialidosis; Galactosialidosis; Gm2-Gangliosidosis, Variant B1; Tay-Sachs Disease; Sandhoff Disease; GM2 Activator DeficiencyLast Updated:November 12, 2020Recruiting
Condition(s):Fabry DiseaseLast Updated:July 27, 2022Active, not recruiting
Condition(s):Fabry DiseaseLast Updated:November 9, 2023Completed
Condition(s):Fabry DiseaseLast Updated:March 31, 2023Available
Condition(s):MPS I; MPS II; MPS IVA; MPS VI; Mps VII; Gaucher Disease, Type 2; Gaucher Disease, Type 3; Pompe Disease Infantile-Onset; Wolman DiseaseLast Updated:September 21, 2023Recruiting
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