Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Muscular Dystrophy, Type 2E (LGMD2E) (Beta-Sarcoglycan Deficiency)
Condition(s):Limb-Girdle Muscular Dystrophy, Type 2ELast Updated:February 13, 2024Active, not recruiting