Adeno-Associated Virus (AAV) Antibody Study in Subjects OTC Deficiency, GSDIa, and Wilson Disease
Condition(s):Ornithine Transcarbamylase Deficiency; Wilson Disease; Glycogen Storage Disease Type IALast Updated:June 12, 2023Terminated
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Condition(s):Ornithine Transcarbamylase Deficiency; Wilson Disease; Glycogen Storage Disease Type IALast Updated:June 12, 2023Terminated
Condition(s):Ornithine Transcarbamylase (OTC) DeficiencyLast Updated:January 25, 2024Active, not recruiting
Condition(s):MedulloblastomaLast Updated:September 28, 2023Recruiting
Condition(s):BurnsLast Updated:January 13, 2017Withdrawn
Condition(s):Brain Diseases, Metabolic, Inborn; Urea Cycle Disorder; Ornithine Transcarbamylase DeficiencyLast Updated:June 24, 2015Completed
Condition(s):Pulmonary Disease, Chronic ObstructiveLast Updated:April 11, 2019Unknown status
Condition(s):Acute on Chronic Liver Failure; Traditional Chinese Medicine; Hepatitis BLast Updated:March 31, 2022Completed
Condition(s):HealthyLast Updated:January 9, 2018Completed
Condition(s):Urea Cycle Disorder; Organic Acidemia; Maple Syrup Urine Disease; Glutaric Acidemia I; Fatty Acid Oxidation Disorder; Hypoxic-Ischemic EncephalopathyLast Updated:February 7, 2024Recruiting
Condition(s):Urea Cycle Disorder; Lysinuric Protein IntoleranceLast Updated:September 28, 2023Completed
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