Betaine and Peroxisome Biogenesis Disorders
Condition(s):Peroxisome Biogenesis DisordersLast Updated:June 28, 2016Completed
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Condition(s):Peroxisome Biogenesis DisordersLast Updated:June 28, 2016Completed
Condition(s):Zellweger SpectrumLast Updated:October 16, 2019Completed
Condition(s):Zellweger Spectrum DisorderLast Updated:January 5, 2024Recruiting
Condition(s):Peroxisome Biogenesis Disorder; Zellweger Spectrum Disorder; RCDP – Rhizomelic Chondrodysplasia Punctata; D-Bifunctional Protein Deficiency; Alpha-Methylacyl-CoA Racemase Deficiency; Peroxisomal Acyl-CoA Oxidase Deficiency; Peroxisomal Acyl-CoA Oxidase 2 Deficiency; ATP Binding Cassette Subfamily D Member 3 Gene Mutation; ACBD5 (AcylCoA Binding Domain 5) Deficiency; Adult Refsum Disease; Sterol Carrier Protein 2 DeficiencyLast Updated:October 31, 2023Recruiting
Condition(s):Zellweger Syndrome; Peroxisome Biogenesis DisordersLast Updated:December 17, 2020Completed
Condition(s):Bile Acid Synthesis DisordersLast Updated:October 2, 2023Active, not recruiting
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