AAVRh.10 Administered to Children With Late Infantile Neuronal Ceroid Lipofuscinosis
Condition(s):Late Infantile Neuronal Ceroid Lipofuscinosis; Batten DiseaseLast Updated:August 31, 2020Completed
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Condition(s):Late Infantile Neuronal Ceroid Lipofuscinosis; Batten DiseaseLast Updated:August 31, 2020Completed
Condition(s):Gaucher Disease, Type 3Last Updated:June 11, 2021Completed
Condition(s):Juvenile Neuronal Ceroid LipofuscinosisLast Updated:May 21, 2019Completed
Condition(s):Familial Partial Lipodystrophy; Hypertriglyceridemia; Fatty Liver; NASH – Nonalcoholic SteatohepatitisLast Updated:August 17, 2020Completed
Condition(s):Gaucher’s DiseaseLast Updated:March 4, 2008Completed
Condition(s):Fabry DiseaseLast Updated:June 24, 2016Completed
Condition(s):Fabry DiseaseLast Updated:July 10, 2014Completed
Condition(s):Fabry DiseaseLast Updated:May 28, 2014Completed
Condition(s):Familial HypercholesterolemiaLast Updated:September 23, 2016Withdrawn
Condition(s):Gaucher DiseaseLast Updated:June 28, 2021Completed
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