Hereditary Central Nervous System Demyelinating Diseases: 113 Clinical Trials, Page 1 of 12

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Natural History Study of Children With Metachromatic Leukodystrophy

Condition(s):Lipid Metabolism Disorders; Metachromatic Leukodystrophy (MLD); Nervous System Diseases; Brain Diseases; Central Nervous System Diseases; Demyelinating Diseases; Metabolism, Inborn Errors; Genetic Diseases, Inborn; Sphingolipidoses; Hereditary Central Nervous System Demyelinating Diseases; Metabolic Inborn Brain Diseases; Lysosomal Storage Diseases; Metabolic Diseases; SulfatidosisLast Updated:March 17, 2021Terminated

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