First-in-Human Study of TSHA-101 Gene Therapy for Treatment of Infantile Onset GM2 Gangliosidosis
Condition(s):Infantile GM2 Gangliosidosis (Disorder)Last Updated:May 9, 2023Active, not recruiting
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Condition(s):Infantile GM2 Gangliosidosis (Disorder)Last Updated:May 9, 2023Active, not recruiting
Condition(s):Gangliosidoses, GM2; Sandhoff Disease; Tay-Sachs DiseaseLast Updated:February 23, 2012Completed
Condition(s):GM1 Gangliosidosis; GM2 Gangliosidosis; Gaucher Disease, Type 2; Tay-Sachs Disease; AB Variant Gangliosidosis GM2; Sandhoff DiseaseLast Updated:November 8, 2021Completed
Condition(s):GM2 Gangliosidosis; Niemann-Pick Disease, Type CLast Updated:February 26, 2024Active, not recruiting
Condition(s):GM2 Gangliosidosis; Tay-Sachs Disease; Sandhoff DiseaseLast Updated:March 12, 2024Completed
Condition(s):GM2 GangliosidosisLast Updated:September 10, 2020Unknown status
Condition(s):Gangliosidoses GM2Last Updated:May 19, 2016Completed
Condition(s):GM2 Gangliosidoses; Tay-Sachs; Sandhoff DiseaseLast Updated:May 6, 2008Completed
Condition(s):GM2 Gangliosidosis; Supportive CareLast Updated:April 25, 2023Recruiting
Condition(s):G(M2) Ganglioside; Tay-Sachs Disease Ganglioside; Sandhoff Disease GangliosideLast Updated:February 25, 2013Withdrawn
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