Long-Term Follow-Up Gene Therapy Study for Achromatopsia CNGB3 and CNGA3
Condition(s):AchromatopsiaLast Updated:March 15, 2024Active, not recruiting
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Condition(s):AchromatopsiaLast Updated:March 15, 2024Active, not recruiting
Condition(s):AchromatopsiaLast Updated:March 8, 2023Completed
Condition(s):AchromatopsiaLast Updated:June 27, 2023Completed
Condition(s):AchromatopsiaLast Updated:December 8, 2022Recruiting
Condition(s):AchromatopsiaLast Updated:July 22, 2022Active, not recruiting
Condition(s):AchromatopsiaLast Updated:October 13, 2017Completed
Condition(s):Eye Disease; AchromatopsiaLast Updated:November 21, 2016Completed
Condition(s):Age Related Macular Degeneration; Retinitis Pigmentosa; Congenital Stationary Night Blindness; ColorblindnessLast Updated:September 21, 2016Completed
Condition(s):Increased Lordosis/Scoliosis; Hyporeflexia; Duchenne Muscular Dystrophy; Red-Green Color Blindness; Lordosis; Scoliosis; Muscular Atrophy; Muscular WeaknessLast Updated:March 24, 2022Completed
Condition(s):Eye Diseases Hereditary; Retinal Disease; Achromatopsia; Bardet-Biedl Syndrome; Bassen-Kornzweig Syndrome; Batten Disease; Best Disease; Choroidal Dystrophy; Choroideremia; Cone Dystrophy; Cone-Rod Dystrophy; Congenital Stationary Night Blindness; Enhanced S-Cone Syndrome; Fundus Albipunctatus; Goldmann-Favre Syndrome; Gyrate Atrophy; Juvenile Macular Degeneration; Kearns-Sayre Syndrome; Leber Congenital Amaurosis; Refsum Syndrome; Retinitis Pigmentosa; Retinitis Punctata Albescens; Retinoschisis; Rod-Cone Dystrophy; Rod Dystrophy; Rod Monochromacy; Stargardt Disease; Usher SyndromeLast Updated:February 15, 2023Recruiting
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