Clinical Trials Involving Rare Diseases: P
- PANDAS (29)
- PASLI Disease (3)
- PGM1-CDG (4)
- PHACE Syndrome (4)
- PIK3CA-related Overgrowth Spectrum (11)
- PMM2-CDG (CDG-Ia) (4)
- POEMS Syndrome (10)
- PTEN Hamartoma Tumor Syndrome (7)
- Pachydermoperiostosis (1)
- Pachyonychia Congenita (11)
- Paget Disease of the Breast (9)
- Palatopharyngeal Incompetence (14)
- Palindromic Rheumatism (1)
- Pallister-Hall Syndrome (1)
- Palmoplantar Keratoderma (4)
- Pancreatic Adenoma (3)
- Pancreatic Cancer (3,328)
- Pancreatic Neuroendocrine Tumor (159)
- Pantothenate Kinase-associated Neurodegeneration (12)
- Panuveitis (216)
- Papillary Glioneuronal Tumors (3)
- Papillary Renal Cell Carcinoma (57)
- Papillary Thyroid Carcinoma (135)
- Papilledema (27)
- Papillon Lefevre Syndrome (1)
- Paragangliomas 1 (118)
- Parainfluenza Virus Type 3 (13)
- Paramyotonia Congenita (7)
- Paraplegia (144)
- Parapsoriasis (8)
- Parathyroid Carcinoma (17)
- Parkes Weber Syndrome (24)
- Paroxysmal Hemicrania (3)
- Paroxysmal Kinesigenic Choreoathetosis (2)
- Paroxysmal Nocturnal Hemoglobinuria (115)
- Paroxysmal Ventricular Fibrillation (160)
- Pars Planitis (59)
- Parsonage Turner Syndrome (10)
- Partial Atrioventricular Canal (1)
- Partial Deletion of Y (2)
- Patent Ductus Arteriosus (134)
- Pattern Dystrophy (4)
- Pauciarticular Onset Juvenile Idiopathic Arthritis (1)
- Pearson Syndrome (6)
- Pectus Carinatum (15)
- Pediatric Acute-onset Neuropsychiatric Syndrome (8)
- Pediatric Crohn's Disease (53)
- Pediatric Multiple Sclerosis (17)
- Pediatric Ulcerative Colitis (27)
- Pelizaeus-Merzbacher Disease (7)
- Pellucid Marginal Degeneration (9)
- Pemphigus (59)
- Pemphigus Foliaceus (8)
- Pemphigus Vulgaris (35)
- Pemphigus and Fogo Selvagem (2)
- Penile Cancer (78)
- Penis Agenesis (3)
- Pentalogy of Cantrell (3)
- Perilymphatic Fistula (1)
- Peripartum Cardiomyopathy (14)
- Peripheral T-cell Lymphoma (886)
- Periventricular Heterotopia (1)
- Periventricular Leukomalacia (31)
- Permanent Neonatal Diabetes Mellitus (2)
- Perniosis (6)
- Peroxisomal Biogenesis Disorders (68)
- Peroxisome Biogenesis disorder-Zellweger Syndrome Spectrum (5)
- Persistent Genital Arousal Disorder (1)
- Persistent Truncus Arteriosus (5)
- Peters Anomaly (2)
- Peutz-Jeghers Syndrome (18)
- Pfeiffer Syndrome (20)
- Phenylketonuria (139)
- Pheochromocytoma (116)
- Phosphoglycerate Kinase Deficiency (2)
- Phosphoglycerate Mutase Deficiency (1)
- Phosphoserine Aminotransferase Deficiency (1)
- Photosensitive Epilepsy (14)
- Phyllodes Tumor of the Breast (5)
- Piebaldism (5)
- Pierre Robin Sequence (9)
- Pigment-dispersion Syndrome (7)
- Pigmented Villonodular Synovitis (25)
- Pilocytic Astrocytoma (69)
- Pilomatrixoma (2)
- Pineal Germ Cell Tumor (2)
- Pineal Parenchymal Tumors of Intermediate Differentiation (1)
- Pineoblastoma (69)
- Pineocytoma (70)
- Piriformis Syndrome (16)
- Pitt-Hopkins Syndrome (4)
- Pituitary Cancer (4)
- Pituitary Stalk Interruption Syndrome (1)
- Pityriasis Lichenoides (2)
- Pityriasis Lichenoides Chronica (1)
- Pityriasis Rubra Pilaris (4)
- Placenta Disorder (218)
- Plagiocephaly (18)
- Plasma Cell Leukemia (36)
- Plasmablastic Lymphoma (545)
- Plasmacytoma (387)
- Plasminogen Activator Inhibitor Type 1 Deficiency (1)
- Platelet Storage Pool Deficiency (11)
- Pleomorphic Xanthoastrocytoma (16)
- Pleuroparenchymal Fibroelastosis (2)
- Pleuropulmonary Blastoma (8)
- Pneumocystis Jirovecii Pneumonia (119)
- Pneumocystosis (119)
- Poliomyelitis (285)
- Polyarteritis Nodosa (23)
- Polyarticular Onset Juvenile Idiopathic Arthritis (5)
- Polycystic Liver Disease (18)
- Polycythemia Vera (302)
- Polydactyly (6)
- Polyembryoma (17)
- Polymorphic Reticulosis (2)
- Polymyositis (118)
- Polyomavirus Allograft Nephropathy (2)
- Pontocerebellar Hypoplasia (1)
- Pontocerebellar Hypoplasia Type 6 (2)
- Porokeratosis of Mibelli (2)
- Porphyria (57)
- Porphyria Cutanea Tarda (48)
- Posner-Schlossman Syndrome (2)
- Post Polio Syndrome (25)
- Post-transplant Lymphoproliferative Disease (110)
- Post-traumatic Epilepsy (10)
- Posterior Column Ataxia (1)
- Posterior Urethral Valves (9)
- Posterior Uveitis (52)
- Potassium Aggravated Myotonia (2)
- Potocki-Shaffer Syndrome (1)
- Prader-Willi Syndrome (115)
- Precocious Puberty (55)
- Precocious Puberty, Gonadotropin-dependent (1)
- Priapism (9)
- Primary Agammaglobulinemia (23)
- Primary Angiitis of the Central Nervous System (1)
- Primary Biliary Cholangitis (142)
- Primary Carnitine Deficiency (9)
- Primary Central Nervous System Lymphoma (256)
- Primary Ciliary Dyskinesia (55)
- Primary Cutaneous Amyloidosis (3)
- Primary Cutaneous Follicle Center Lymphoma (3)
- Primary Effusion Lymphoma (36)
- Primary Familial Brain Calcification (1)
- Primary Hyperoxaluria Type 1 (41)
- Primary Hyperoxaluria Type 2 (8)
- Primary Hyperoxaluria Type 3 (12)
- Primary Hyperparathyroidism (90)
- Primary Intestinal Lymphangiectasia (1)
- Primary Lateral Sclerosis (731)
- Primary Liver Cancer (256)
- Primary Myelofibrosis (533)
- Primary Orthostatic Hypotension (37)
- Primary Orthostatic Tremor (3)
- Primary Pigmented Nodular Adrenocortical Disease (2)
- Primary Progressive Aphasia (254)
- Primary Sclerosing Cholangitis (117)
- Primary Spontaneous Pneumothorax (36)
- Prinzmetal's Variant Angina (21)
- Progeria (9)
- Progressive Bulbar Palsy (1)
- Progressive Familial Intrahepatic Cholestasis 1 (20)
- Progressive Hemifacial Atrophy (5)
- Progressive Multifocal Leukoencephalopathy (24)
- Progressive Myoclonic Epilepsy (5)
- Progressive Non-fluent Aphasia (17)
- Progressive Supranuclear Palsy (125)
- Progressive Supranuclear Palsy Atypical (4)
- Prolactinoma (25)
- Prolidase Deficiency (1)
- Proliferative Verrucous Leukoplakia (4)
- Proopiomelanocortin Deficiency (4)
- Propionic Acidemia (20)
- Prosthetic Joint Infection (96)
- Proteus Syndrome (7)
- Prothrombin Deficiency (1)
- Protoporphyria (21)
- Prurigo Nodularis (28)
- Pseudoachondroplasia (1)
- Pseudocholinesterase Deficiency (5)
- Pseudohypoaldosteronism Type 2 (4)
- Pseudohypoparathyroidism (17)
- Pseudohypoparathyroidism Type 1A (11)
- Pseudomyxoma Peritonei (30)
- Pseudoneonatal Adrenoleukodystrophy (2)
- Pseudopelade of Brocq (17)
- Pseudopseudohypoparathyroidism (17)
- Pseudoxanthoma Elasticum (24)
- Psoriatic Juvenile Idiopathic Arthritis (11)
- Pterygium of the Conjunctiva and Cornea (1)
- Pudendal Neuralgia (12)
- Pulmonary Arterial Hypertension (688)
- Pulmonary Arteriovenous Malformation (17)
- Pulmonary Atresia With Ventricular Septal Defect (2)
- Pulmonary Edema of Mountaineers (28)
- Pulmonary Surfactant Protein B, Deficiency of (2)
- Pulmonary Valve Stenosis (26)
- Pulmonary Vein Stenosis (7)
- Pulmonary Venoocclusive Disease (2)
- Pulmonary Venous Return Anomaly (5)
- Pulmonic Stenosis (26)
- Punctate Inner Choroidopathy (4)
- Pure Autonomic Failure (67)
- Pure Red Cell Aplasia (67)
- Purine Nucleoside Phosphorylase Deficiency (1)
- Pustular Psoriasis (31)
- Pustulosis Palmaris Et Plantaris (25)
- Pyle Disease (1)
- Pyoderma Gangrenosum (24)
- Pyomyositis (2)
- Pyridoxal 5'-phosphate-dependent Epilepsy (2)
- Pyridoxine Deficiency (4)
- Pyridoxine-dependent Epilepsy (3)
- Pyropoikilocytosis Hereditary (1)
- Pyruvate Carboxylase Deficiency (1)
- Pyruvate Decarboxylase Deficiency (5)
- Pyruvate Dehydrogenase Complex Deficiency (5)
- Pyruvate Dehydrogenase Phosphatase Deficiency (1)
- Pyruvate Kinase Deficiency (13)