Clinical Trials Involving Rare Diseases: N
- N-acetylglutamate Synthase Deficiency (4)
- NBIA/DYT/PARK-PLA2G6 (1)
- Nail-patella Syndrome (1)
- Nakajo Nishimura Syndrome (1)
- Nakajo Syndrome (1)
- Narcolepsy (124)
- Nasopharyngeal Carcinoma (854)
- Necrobiosis Lipoidica (4)
- Necrotizing Autoimmune Myopathy (6)
- Necrotizing Enterocolitis (184)
- Necrotizing Fasciitis (22)
- Neisseria Meningitidis Infection (115)
- Nelson Syndrome (2)
- Nemaline Myopathy (5)
- Neonatal Adrenoleukodystrophy (2)
- Neonatal Herpes (8)
- Neonatal Meningitis (3)
- Neonatal Onset Multisystem Inflammatory Disease (11)
- Neonatal Ovarian Cyst (2)
- Neonatal Stroke (24)
- Neonatal Systemic Lupus Erythematosus (6)
- Nephrocalcinosis (17)
- Nephrogenic Diabetes Insipidus (11)
- Nephrogenic Systemic Fibrosis (16)
- Nephronophthisis (4)
- Nephrosclerosis (6)
- Netherton Syndrome (17)
- Neural Crest Tumor (4)
- Neuroacanthocytosis (1)
- Neuroblastoma (628)
- Neurocutaneous Melanosis (1)
- Neurodegeneration With Brain Iron Accumulation (13)
- Neuroendocrine Carcinoma of the Cervix (2)
- Neuroendocrine Tumor (3,742)
- Neuroepithelioma (7,096)
- Neuroferritinopathy (1)
- Neurofibroma (280)
- Neurofibromatosis (302)
- Neurofibromatosis Type 1 (255)
- Neurofibromatosis Type 2 (55)
- Neurofibromatosis-Noonan Syndrome (1)
- Neurofibrosarcoma (92)
- Neuroleptic Malignant Syndrome (21)
- Neuromyelitis Optica Spectrum Disorder (113)
- Neuronal Ceroid Lipofuscinosis (45)
- Neuronal Ceroid Lipofuscinosis 2 (4)
- Neuronal Ceroid Lipofuscinosis 3 (6)
- Neuronal Ceroid Lipofuscinosis 7 (2)
- Neuronal Intranuclear Inclusion Disease (1)
- Neurosyphilis (4)
- Neurotoxicity Syndromes (244)
- Neutral Lipid Storage Disease With Myopathy (3)
- Nevoid Basal Cell Carcinoma Syndrome (38)
- New Daily-persistent Headache (10)
- Nicolaides-Baraitser Syndrome (1)
- Niemann-Pick Disease (61)
- Niemann-Pick Disease Type A (61)
- Niemann-Pick Disease Type B (1)
- Niemann-Pick Disease Type C1 (56)
- Nijmegen Breakage Syndrome (1)
- Nodding Syndrome (4)
- Nodular Melanoma (4)
- Nodular Regenerative Hyperplasia (20)
- Non 24 Hour Sleep Wake Disorder (9)
- Non Functioning Pancreatic Endocrine Tumor (10)
- Non-Langerhans-Cell Histiocytosis (156)
- Nonbullous Congenital Ichthyosiform Erythroderma (15)
- Nondystrophic Myotonia (8)
- Nonseminomatous Germ Cell Tumor (42)
- Nontuberculous Mycobacterial Lung Disease (19)
- Noonan Syndrome (23)
- Norrie Disease (2)